Smith-Kingsmore syndrome


Smith-Kingsmore syndrome is a rare genetic disorder that is caused by a gain-of-function mutation in a mTOR gene. The facial features of this syndrome are triangular face with a pointed chin, frontal bossing, hypertelorism, eyes with downslanting palpebral fissures, a flat nasal bridge, a long philtrum.

Presentation

The signs of this disease are:
Very frequent:
Frequent:
Occasional:
Very rare:

Cause

The cause of SKS is gain-of-function mutation in a gene MTOR.
This disease is inherited in Autosomal Dominant fashion, but most of the times it's de-novo mutation.

Diagnosis

SKS is a rare condition so many physicians aren't familiar with. A diagnosis of SKS is suspected based upon the identification of symptoms, a patient and family history and a thorough clinical evaluation.
SKS can be confirmed with the detection of a germline or mosaic mutation in the MTOR gene.

Frequency

Frequency of this disease is unknown, but all ethnic groups are equally affected

Treatment

There is no cure for SKS, but management of some symptoms can be achieved

History

SKS was first described by Dr Smith, L.D et al. in 2013.