List of gene therapies
This article contains a list of commercially available gene therapies.
Gene therapies
- Alipogene tiparvovec : AAV-based treatment for lipoprotein lipase deficiency
- Axicabtagene ciloleucel : treatment for large B-cell lymphoma
- Beremagene geperpavec : treatment of wounds.
- Betibeglogene autotemcel : treatment for beta thalassemia
- Brexucabtagene autoleucel : treatment for mantle cell lymphoma and acute lymphoblastic leukemia
- Cambiogenplasmid : treatment for vascular endothelial growth factor peripheral artery disease
- Ciltacabtagene autoleucel : treatment for multiple myeloma
- Delandistrogene moxeparvovec : treatment for Duchenne muscular dystrophy
- Elivaldogene autotemcel : treatment for cerebral adrenoleukodystrophy
- Etranacogene dezaparvovec : AAV-based treatment for hemophilia B
- Exagamglogene autotemcel : treatment for sickle cell disease.
- Gendicine: treatment for head and neck squamous cell carcinoma
- Idecabtagene vicleucel : treatment for multiple myeloma
- Lovotibeglogene autotemcel : treatment for sickle cell disease.
- Nadofaragene firadenovec : treatment for bladder cancer
- Obecabtagene autoleucel : treatment of acute lymphoblastic leukemia
- Onasemnogene abeparvovec : AAV-based treatment for spinal muscular atrophy
- Prademagene zamikeracel : recessive dystrophic epidermolysis bullosa
- Revakinagene taroretcel : treatment of macular telangiectasia type 2
- Strimvelis: treatment for adenosine deaminase deficiency
- Talimogene laherparepvec : treatment for melanoma in people who have recurring skin lesions
- Tisagenlecleucel : treatment for B cell lymphoblastic leukemia
- Valoctocogene roxaparvovec : treatment for hemophilia A
- Voretigene neparvovec : AAV-based treatment for Leber congenital amaurosis